An investigational in vivo base editing medicine targeting ANGPTL3, VERVE-201, achieves precise and durable liver editing in nonclinical studies
图像编辑
体内
医学
计算机科学
生物
人工智能
遗传学
图像(数学)
作者
Richard Lee,Anne Marie Mazzola,Jamie Denizio,Taiji Mizoguchi,Victoria Clendaniel,Ryan Garrity,Nicholas Cox,Zachary Glass,Hareesh Chamarthi,Sydney Flannigan,Yuri Matsumoto,Maurine Braun,Sekar Kathiresan,Joseph C. Biedenkapp,Ellen Rohde,Andrew M. Bellinger,Amit V. Khera