KIT‐mutated pediatric core‐binding factor systemic mastocytosis‐acute myeloid leukemia treated with avapritinib and decitabine

医学 癌症 老年学 内科学
作者
Irtiza Sheikh,Shaikha Alqahtani,C. Cameron Yin,David McCall,Branko Cuglievan,Dristhi Ragoonanan,Jeremy Connors,Amber Gibson,César Núnêz,Michael Roth,Maro Ohanian,Gautam Borthakur,Miriam B. Garcia
出处
期刊:Pediatric Blood & Cancer [Wiley]
卷期号:71 (4) 被引量:1
标识
DOI:10.1002/pbc.30898
摘要

Pediatric Blood & CancerVolume 71, Issue 4 e30898 LETTER TO THE EDITOR KIT-mutated pediatric core-binding factor systemic mastocytosis-acute myeloid leukemia treated with avapritinib and decitabine Irtiza N. Sheikh, Irtiza N. Sheikh orcid.org/0000-0003-4869-8818 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorShaikha AlQahtani, Shaikha AlQahtani orcid.org/0009-0004-1176-8952 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorC. Cameron Yin, C. Cameron Yin Department of Hematopathology, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorDavid McCall, David McCall orcid.org/0000-0003-2297-9670 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorBranko Cuglievan, Branko Cuglievan Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorDristhi Ragoonanan, Dristhi Ragoonanan orcid.org/0000-0002-8199-9404 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorJeremy S. Connors, Jeremy S. Connors Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorAmber Gibson, Amber Gibson orcid.org/0000-0002-9146-4702 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorCesar Nunez, Cesar Nunez Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorMichael Roth, Michael Roth orcid.org/0000-0002-6411-8353 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorMaro Ohanian, Maro Ohanian Department of Leukemia, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorGautam Borthakur, Gautam Borthakur Department of Leukemia, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorMiriam B. Garcia, Corresponding Author Miriam B. Garcia [email protected] orcid.org/0000-0002-2978-2267 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USA Correspondence Miriam B. Garcia, Department of Pediatrics, The University of Texas MD Anderson Cancer Center, 1515 Holcombe Blvd, Unit 87, Houston, TX 77030, USA. Email: [email protected]Search for more papers by this author Irtiza N. Sheikh, Irtiza N. Sheikh orcid.org/0000-0003-4869-8818 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorShaikha AlQahtani, Shaikha AlQahtani orcid.org/0009-0004-1176-8952 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorC. Cameron Yin, C. Cameron Yin Department of Hematopathology, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorDavid McCall, David McCall orcid.org/0000-0003-2297-9670 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorBranko Cuglievan, Branko Cuglievan Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorDristhi Ragoonanan, Dristhi Ragoonanan orcid.org/0000-0002-8199-9404 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorJeremy S. Connors, Jeremy S. Connors Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorAmber Gibson, Amber Gibson orcid.org/0000-0002-9146-4702 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorCesar Nunez, Cesar Nunez Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorMichael Roth, Michael Roth orcid.org/0000-0002-6411-8353 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorMaro Ohanian, Maro Ohanian Department of Leukemia, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorGautam Borthakur, Gautam Borthakur Department of Leukemia, The University of Texas MD Anderson Cancer Center, Houston, Texas, USASearch for more papers by this authorMiriam B. Garcia, Corresponding Author Miriam B. Garcia [email protected] orcid.org/0000-0002-2978-2267 Department of Pediatrics, The University of Texas MD Anderson Cancer Center, Houston, Texas, USA Correspondence Miriam B. Garcia, Department of Pediatrics, The University of Texas MD Anderson Cancer Center, 1515 Holcombe Blvd, Unit 87, Houston, TX 77030, USA. Email: [email protected]Search for more papers by this author First published: 30 January 2024 https://doi.org/10.1002/pbc.30898 Abstract was submitted for publication to the American Society of Pediatric Hematology/Oncology Conference, April 2024, Seattle, Washington. Read the full textAboutPDF ToolsRequest permissionExport citationAdd to favoritesTrack citation ShareShare Give accessShare full text accessShare full-text accessPlease review our Terms and Conditions of Use and check box below to share full-text version of article.I have read and accept the Wiley Online Library Terms and Conditions of UseShareable LinkUse the link below to share a full-text version of this article with your friends and colleagues. Learn more.Copy URL Share a linkShare onEmailFacebookTwitterLinkedInRedditWechat REFERENCES 1Gogia A, Sharawat SK, Kumar R, Sarkar C, Bakhshi S. Systemic mastocytosis associated with childhood acute myeloid leukemia. J Pediatr Hematol Oncol. 2013; 35(2): 163-164. doi:10.1097/MPH.0b013e318253f060 10.1097/MPH.0b013e318253f060 PubMedWeb of Science®Google Scholar 2Mahadeo KM, Wolgast L, McMahon C, Cole PD. Systemic mastocytosis in a child with t(8;21) acute myeloid leukemia. 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Safety and efficacy of avapritinib in advanced systemic mastocytosis: the phase 1 EXPLORER trial. Nat Med. 2021; 27(12): 2183-2191. doi:10.1038/s41591-021-01538-9 10.1038/s41591-021-01538-9 CASPubMedWeb of Science®Google Scholar 18 FDA approves avapritinib for advanced systemic mastocytosis. FDA; 2021. Accessed August 29, 2023. https://www.fda.gov/drugs/resources-information-approved-drugs/fda-approves-avapritinib-advanced-systemic-mastocytosis Google Scholar Volume71, Issue4April 2024e30898 ReferencesRelatedInformation
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