医学
遗传增强
子宫内
疾病
胎儿
产前诊断
怀孕
临床试验
基因
生物信息学
病理
遗传学
生物
作者
Marisa E. Schwab,Tippi C. MacKenzie
出处
期刊:Clinical Obstetrics and Gynecology
[Ovid Technologies (Wolters Kluwer)]
日期:2021-10-06
卷期号:64 (4): 876-885
被引量:11
标识
DOI:10.1097/grf.0000000000000655
摘要
Prenatal gene therapy could provide a cure for many monogenic diseases. Prenatal gene therapy has multiple potential advantages over postnatal therapy, including treating before the onset of disease, the ability to induce tolerance and cross the blood-brain barrier. In this chapter, we will describe in utero gene therapy and its rationale, clinical trials of postnatal gene therapy, preclinical studies of in utero gene therapy, and potential risks to the mother and fetus.
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