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2022-10-31 加入
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Involvement of the Sodium Channel Nav1.7 in Paclitaxel-induced Peripheral Neuropathy through ERK1/2 Signaling in Rats
16小时前
求助中
Biodistribution and Tolerability of AAV-PHP.B-CBh-SMN1 in Wistar Han Rats and Cynomolgus Macaques Reveal Different Toxicologic Profiles
3天前
已完结
Intravitreal Delivery of rAAV2tYF-CB-hRS1 Vector for Gene Augmentation Therapy in Patients with X-Linked Retinoschisis
13天前
已完结
RGX-202, an Investigational Gene Therapy for the Treatment of Duchenne Muscular Dystrophy: Interim Clinical Data (S21.005)
20天前
已关闭
Brainwide silencing of prion protein by AAV-mediated delivery of an engineered compact epigenetic editor
21天前
已完结
Gene therapy for neovascular age-related macular degeneration by subretinal delivery of RGX-314: a phase 1/2a dose-escalation study
1个月前
已完结
α-Galactosidase A deficiency. Fabry disease
1个月前
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Effects of enzyme replacement therapy on the cardiomyopathy of Anderson Fabry disease: a randomised, double-blind, placebo-controlled clinical trial of agalsidase alfa
1个月前
已完结
Mobility Testing and Other Performance-Based Assessments of Functional Vision in Patients with Inherited Retinal Disease
2个月前
已完结
[Clinical analysis of 10 patients with Fabry disease]
2个月前
已完结
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