Lv1
26 积分 2022-09-15 加入
异染性脑白质营养不良
6天前
已完结
AAV-Mediated Gene Transfer of WDR45 Corrects Neurological Deficits in the Mouse Model of Beta-Propeller Protein-Associated Neurodegeneration
9天前
已完结
Beyond ISGlylation: Functions of Free Intracellular and Extracellular ISG15
10天前
已完结
Safety profile of the first pediatric cardiomyopathy gene therapy trial: RP-A501 (AAV9: LAMP2B) for Danon disease
16天前
已完结
Mendelian inheritance revisited: dominance and recessiveness in medical genetics
16天前
已完结
Primary mitochondrial diseases: The intertwined pathophysiology of bioenergetic dysregulation, oxidative stress and neuroinflammation
25天前
已完结
A comprehensive study of AAV tropism across C57BL/6 mice, BALB/c mice, and crab-eating macaques
1个月前
已完结
Evaluation of safety and early efficacy of AAV gene therapy in mouse models of vanishing white matter disease
2个月前
已完结
Capsid-Engineering for Central Nervous System-Directed Gene Therapy with Adeno-Associated Virus Vectors
2个月前
已完结
Leukoencephalopathy with Brain Stem and Spinal Cord Involvement and Lactate Elevation
4个月前
已关闭
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