Betibeglogene Autotemcel (Beti-cel) Gene Addition Therapy Results in Durable Hemoglobin A (HbA) Production with up to 10 Years of Follow-up in Participants with Transfusion-Dependent β-Thalassemia
地中海贫血
血红蛋白
医学
内科学
作者
Timothy S. Olson,Alexis A. Thompson,Janet L. Kwiatkowski,Jennifer Schneiderman,Isabelle Thuret,Andreas E. Kulozik,Evangelia Yannaki,Marina Cavazzana,Suradej Hongeng,Martin G. Sauer,Adrian J. Thrasher,Ashutosh Lal,John E.J. Rasko,Hancheng Jiang,Tao Ge,Himal L. Thakar,Niki Witthuhn,Mark C. Walters,Franco Locatelli