Nonclinical evidence supports efficacy of Ixo-vec gene therapy for nAMD at a dose of 3E10 vg/eye (6E10 vg/eye human equivalent dose) and demonstrates feasibility of staggered dosing in contralateral eyes
加药
人眼
医学
眼科
药理学
物理
光学
作者
Kris Poulsen,Kelly Hanna,Julio Nieves,Ngoc Nguyen,Pallavi Sharma,Ruslan N. Grishanin,Romu Corbau,Szilárd Kiss