医学
心脏病学
肥厚性心肌病
内科学
梗阻性心肌病
作者
Martin S. Maron,Ahmad Masri,Michael E. Nassif,Roberto Barriales‐Villa,Michael Arad,Nuno Cardim,Lubna Choudhury,Brian Claggett,Caroline Coats,Hans‐Dirk Düngen,Pablo García‐Pavía,Albert Hagège,James L. Januzzi,Matthew M.Y. Lee,Gregory D. Lewis,Changsheng Ma,Michelle Michels,Iacopo Olivotto,Artur Oręziak,Anjali Owens
标识
DOI:10.1056/nejmoa2401424
摘要
Among patients with symptomatic obstructive HCM, treatment with aficamten resulted in a significantly greater improvement in peak oxygen uptake than placebo. (Funded by Cytokinetics; SEQUOIA-HCM ClinicalTrials.gov number, NCT05186818.).
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