遗传增强
疾病
生物
病毒载体
重症监护医学
载体(分子生物学)
基因
生物信息学
医学
遗传学
内科学
重组DNA
作者
Clare E. Thomas,Anja Ehrhardt,Mark A. Kay
摘要
Gene therapy has a history of controversy. Encouraging results are starting to emerge from the clinic, but questions are still being asked about the safety of this new molecular medicine. With the development of a leukaemia-like syndrome in two of the small number of patients that have been cured of a disease by gene therapy, it is timely to contemplate how far this technology has come, and how far it still has to go.
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