遗传性血管水肿
血管性水肿
前激肽释放酶
医学
C1抑制剂
激肽释放酶
免疫学
皮肤病科
化学
生物化学
酶
作者
M. Riedl,Raffi Tachdjian,William R. Lumry,Timothy Craig,Gül Karakaya,Aslı Gelincik,Marcin Stobiecki,Joshua Jacobs,Nihal Mete,Avner Reshef,Mark Gompels,Michael Manning,Laura Bordone,Ken B. Newman,Sabrina Treadwell,Sophie X. Wang,Aaron Yarlas,Danny M. Cohn
标识
DOI:10.1056/nejmoa2402478
摘要
Donidalorsen treatment reduced the hereditary angioedema attack rate, a finding that supports potential prophylactic use for hereditary angioedema. (Funded by Ionis Pharmaceuticals; OASIS-HAE ClinicalTrials.gov number, NCT05139810.).
科研通智能强力驱动
Strongly Powered by AbleSci AI