遗传性血管水肿
血管性水肿
前激肽释放酶
医学
C1抑制剂
激肽释放酶
免疫学
皮肤病科
化学
生物化学
酶
作者
Marc Riedl,Raffi Tachdjian,William R. Lumry,Timothy Craig,Gül Karakaya,Aslı Gelincik,Marcin Stobiecki,Joshua Jacobs,Nihal Mete,Avner Reshef,Mark Gompels,Michael E. Manning,Laura Bordone,Ken B. Newman,Sabrina Treadwell,Sophie X. Wang,Aaron Yarlas,Danny M. Cohn
标识
DOI：10.1056/nejmoa2402478
摘要
Hereditary angioedema is a rare disorder characterized by episodic, potentially life-threatening swelling caused by kallikrein-kinin dysregulation. Long-term prophylaxis can stabilize this system. Donidalorsen, an antisense oligonucleotide, specifically reduces prekallikrein expression.
科研通智能强力驱动
Strongly Powered by AbleSci AI
爱静静
Singularity
HEIKU
Hayat
shinysparrow
不配.
云瑾
curtisness
kento
zzzyyy
Henry
rosalieshi
浅尝离白
徐叽钰
zyfqpc
元谷雪
8R60d8
我不是BOB
pluto
tuanheqi
皖公网安备34019202002308
